RNA-targeting Therapeutics for non-experts 

 

     January 23rd @ 8AM PST 

 

       Sign up here       

 

1-hour course designed for anyone working to bring new hope to rare disease patients  

 Free software license for managing and developing your own therapeutics  

 Free office hours for Q&A 

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What’s included:

• The basics of RNA-targeting therapeutics chemistry 

• Real-world strategies used in rare disease drug development

• How to turn harmful genes down

• How turn helpful genes up

• Fix splicing errors that cause disease

• Reduce unwanted side effects through smarter design

• An introduction to siRNA and single stranded antisense therapies

• Clinical examples:  SMA, DMD and ALS

 

Price $1,500